Ultragenyx is a brand that is dedicated to transforming the lives of individuals who are living with rare and ultrarare diseases. They are focused on developing groundbreaking treatments for these conditions, with the aim of moving the rare disease community forward. This commitment is evident in their dedication to the development and delivery of treatments for rare diseases, where none currently exist.

Ultragenyx employs a multi-faceted approach in their quest to develop therapies for rare and ultrarare genetic diseases. They explore various drug modalities to identify the best treatment strategy for each specific genetic disease they are studying. Their science-driven approach is supported by a robust gene therapy platform and an extensive pipeline of potential treatments for different rare diseases.

In addition to their focus on research and development, Ultragenyx is passionate about patient advocacy and ensuring access to their therapies. They work closely with the rare disease community, providing grants, contributions, and early access programs to support patients. To achieve their goals, Ultragenyx has assembled a talented team and developed a people-first culture.

They are consistently seeking passionate individuals to join them in their mission. To stay up-to-date with Ultragenyx's latest developments, news releases, presentations, and blog posts are available on their Newsroom page. Ultragenyx's commitment to advancing innovative medicines for rare diseases is underpinned by their strong leadership team, led by Chief Executive Officer and President, Emil D.

Kakkis, M. D., Ph. D.

Overall, Ultragenyx is a brand that is driven by a purpose to make a meaningful impact on the lives of individuals living with rare diseases. Their dedication to research, patient advocacy, and a people-first culture sets them apart in the field of rare disease treatment