Ultragenyx is a leading brand dedicated to developing innovative treatments for rare and ultrarare diseases. With a strong focus on patient advocacy, Ultragenyx aims to transform the lives of as many people as possible who are living with these rare conditions. They are committed to the development and delivery of therapies for rare diseases where currently no treatments exist.

Ultragenyx employs a wide range of drug modalities to discover the most effective treatment strategies for each genetic disease they study. Their pipeline of therapies is one of the largest and most diverse in the field of rare diseases. Some of the genetic diseases they are targeting include GSDIa, OTC Deficiency, Wilson Disease, OI, AS, GSD III, MPS IIIA, and CDD.

Led by a team of passionate biopharmaceutical leaders, Ultragenyx combines deep expertise in drug development and commercialization. They prioritize the well-being and needs of rare disease communities, striving to make a meaningful difference in the lives of patients. Join Ultragenyx on their mission to advance medicines for rare diseases and make a positive impact in the world