Orphanix is a brand that is dedicated to improving the lives of newborns with rare diseases. Their mission is to fill the blind spots in pediatric medicinal care by providing safe, innovative, and easily accessible medical solutions. They strive to understand the needs of affected babies and create innovative opportunities for treatment.

Orphanix identifies, develops, and commercializes orphan drugs across all pediatric indications, based on a thorough evaluation of academic and real-world data. They focus on indications where there is a high unmet medical need, a high level of clinical evidence, and no available adequate products for specific rare diseases. Orphanix aims to gain intellectual property rights and orphan designations from authorities like the FDA and EMA, which ensures market exclusivity after authorization.

They also collaborate with fully integrated pharmaceutical companies to complement their portfolios and develop solutions for high unmet medical needs. With their expertise and commitment, Orphanix is filling the blind spots in pediatric rare disease care with effective orphan medicines