Spark Therapeutics is a leading biotechnology company that specializes in gene therapy. With a strong focus on research and development, Spark Therapeutics aims to treat and possibly prevent diseases using innovative gene therapy techniques. Gene therapy has been studied for over 50 years, and Spark Therapeutics is at the forefront of this exciting field.

The company utilizes adeno-associated viral (AAV) vectors as a delivery system to target specific cells in the body, such as the retina, liver, and central nervous system. By introducing new or functional genes, Spark Therapeutics aims to restore the normal function of mutated genes. One of the highlights of Spark Therapeutics is their in-house, highly specialized manufacturing process for producing AAV vectors that encapsulate genetic material for the potential treatment of genetic diseases.

This ensures the highest quality and safety standards for their therapies. Overall, Spark Therapeutics is dedicated to advancing the field of gene therapy and providing hope for patients and their families. Through their innovative research and commitment to excellence, they continue to pave the way for groundbreaking treatments in the field of genetic diseases