Ionis

Ionis Trials is the clinical study information platform of Ionis Pharmaceuticals, Inc., a company developing medicines with an antisense RNA-targeted drug discovery platform. Its research spans neurology, cardiometabolic disease, and other therapeutic areas, with a focus on investigating potential treatments for conditions that may have limited options. The site helps patients and families discover studies, review study purposes and phases, and find links to ClinicalTrials.gov or study sites. It also invites people to inquire about opportunities to participate.

Featured and enrolling research includes studies involving Angelman syndrome, Dravet syndrome, MECP2 duplication syndrome, and Pelizaeus-Merzbacher disease, as well as conditions such as transthyretin-mediated amyloid cardiomyopathy, hypertriglyceridemia, familial chylomicronemia syndrome, and hereditary angioedema. The portfolio includes interventional clinical trials at multiple phases and observational research assessing disease measures and real-world treatment outcomes. Ionis Trials also directs visitors to information about past and ongoing Ionis studies and offers educational resources to help people stay informed about research and advances in healthcare.